© 2023 MJH Life Sciences™ and Managed Healthcare Executive. All rights reserved.
Hemophilia
FDA Approves Hemgenix, $3.5 million Gene Therapy for Hemophilia B
November 23, 2022
Payers are bracing themselves for more ultra-expensive gene therapies.
New Line of Gene Therapy Vectors Better at Targeting Liver Cells in Hemophilia B
November 21, 2022
German researchers developed a modified adeno-associated virus capsid that has greater affinity for liver cells.
Dutch Company Raises Over $12 Million for Development of Home-based Blood Coagulation Test
November 17, 2022
Enyzyre says its at-home testing system will be a major advance for people with hemophilia because they will better able to manage the disease on their own.
Gene Therapy for Hemophilia Is on the Brink of FDA Approval
November 17, 2022
CSL Behring's gene therapy, called EntranaDez, may be approved later this month. BioMarin, Pfizer, Bayer and Freeline Therapeutics also have gene therapies for hemophilia in development.
Treatment for Hemophilia: Many Decisions, Some Difficult, All Should Be Shared
October 04, 2022
The hemophilia organization developed a shared decision-making tool for patients and providers.
Judging Up-and-Coming Hemophilia Treatments
October 04, 2022
Long-acting recombinant replacement factor gets favorable rating from multidisciplinary group. Gene therapy was viewed with some wariness.
Diabetes and HIV May Increase Risk of Hypertension in People with Hemophilia
September 21, 2022
Findings suggest that screening people with hemophilia for diabetes and hypertension might have benefits.
Gene Therapy for Severe Hemophilia B Could Be More Cost Effective Than Current Treatments
September 19, 2022
An analysis found that a single dose of gene therapy would be more cost-effective than on-demand or prophylaxis factor replacement in 92% of cases.
Gene Therapies for Hemophilia. Possibly Curative, Likely Ultraexpensive
September 08, 2022
Three gene therapies in late-stage development are designed to supply working copies of genes that people with hemophilia are missing. They may be one-time, curative treatments, but the seven-figure price tags will be an issue.
Anxiety, Depression, and Diabetes Higher in Older Males with Hemophilia; Cardiovascular Disease Lower
August 19, 2022
Lack of blood clotting may afford some protection against common cardiovascular disease events, such as ischemic stroke.