December 21st 2023
Men with severe or moderately severe hemophilia B continue to display low bleeding rates and very little use of replacement therapies for at least three years following a single dose of the approved gene therapy hemgenix.
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May 31, 2024 - June 2, 2024
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6th Annual Precision Medicine Symposium: An Illustrated Tumor Board
October 18-19, 2024
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42nd Annual CFS®: Innovative Cancer Therapy for Tomorrow®
November 13-15, 2024
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41st Annual CFS®: Innovative Cancer Therapy for Tomorrow
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Community Practice Connections™: 5th Annual Precision Medicine Symposium – An Illustrated Tumor Board
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Gene Therapies for Hemophilia. Possibly Curative, Likely Ultraexpensive
September 8th 2022Three gene therapies in late-stage development are designed to supply working copies of genes that people with hemophilia are missing. They may be one-time, curative treatments, but the seven-figure price tags will be an issue.
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