
|Articles|May 4, 2023
The Latest Trends and Potential Implications in Rare Disease, Orphan Drug Management | Asembia Specialty Pharmacy Summit
Author(s)Peter Wehrwein, Managing Editor
Ed Paiewonsky, Director, Medical Outcomes Science Liaison at Alnylam Pharmaceuticals, discussed results of the Alnylam Rare Disease Trend report at this year's Asembia Specialty Pharmacy Summit.
Advertisement
Results of the Alnylam Rare Disease Trend report were shared at this year's Asembia Specialty Pharmacy Summit.
Some key rare disease trends include the increased focus in rare disease management, sites of care policies increasing, uncertainty around recent federal legislation and how these changes will affect payers and rare disease industry.
Newsletter
Get the latest industry news, event updates, and more from Managed healthcare Executive.
Advertisement
Advertisement
Advertisement
Trending on Managed Healthcare Executive
1
How new psoriasis, alopecia and atopic dermatitis therapies stood out at Fall Clinical Derm 2025
2
UC Davis develops new drug for bladder cancer patients
3
The FDA proposes ditching comparative efficacy studies for biosimilars
4
Misdiagnosis of Type 1 diabetes remains a major problem, despite advances
5

















































